Empowering the lives of patients with rare diseases
Life is a health journey for patients affected by rare diseases. The rarity and complexity of these conditions can make them difficult to diagnose and treat. This can take both a physical and emotional toll on patients and their families.
Sanofi Genzyme, has been a pioneer in rare diseases for more than 35 years by developing enzyme replacement therapies for the treatment of lysosomal storage disorders. Our expertise in the development of therapies for rare diseases that can be progressive, severely debilitating and life-threatening started with lysosomal storage disorders including Gaucher, Fabry, MPS I and Pompe diseases. This is still an important focus for us and we have also expanded our focus to include related conditions where high unmet medical need exists.
We continue to focus on being transformative in rare diseases: developing therapies, supporting research and offering innovative solutions that have the potential to offer meaningful change to those impacted by rare diseases. Our commitment to provide patients, with healthcare solutions goes beyond product to offering services and support that complement our therapies.